Hemophilia at a Glance

Hemophilia Toolkit

Overview of Hemophilia: Hemophilia at a Glance

“When it comes to hemophilia we tend to focus on cost and it’s really education that’s needed; this is where the toolkit provides a lot of value. With education we can better understand waste factors to bring costs down.”

- MBGH Employer Member

Understanding Hemophilia’s Impact

Hemophilia is a rare genetic bleeding disorder that affects over 30,000 people in the U.S. and requires a lifetime of intensive management and individualized care strategies by both the health care team and patient. Despite significant advancements in treatment—allowing most employees with hemophilia to lead full, active professional lives—the condition remains complex, costly, and often misunderstood within the employer community.

It is an important driver of employer health care costs, ranking among the top 20 highest-cost claims conditions. Total annual health care costs can be up to 25 times more for a person living with hemophilia compared to members who don’t live with this condition. The annual cost of factor therapy for a person with severe hemophilia is roughly $300,000 with total medical costs often far exceeding that amount.

Factor replacement therapy is the primary treatment for hemophilia to replace or bypass missing blood proteins. It enables proper blood clotting, either preventing bleeds (prophylaxis) or stopping active bleeds (on demand). The recommended frequency of administration varies between products.

The financial burden is only part of the challenge. Hemophilia can cause recurrent joint bleeds that lead to chronic pain, reduced mobility, and long-term musculoskeletal damage. These complications often require time away from work for treatment, recovery, medical appointments, or emergency care. Even when at work, individuals may experience a lack of concentration, fear and anxiety, fatigue, and limited stamina, affecting their ability to perform physically demanding tasks. Employers may need to modify duties, offer flexible schedules, and/or support remote work to maintain productivity and safety.

Employees with hemophilia may need short, unplanned periods away from work to manage sudden bleeds. The U.S. Department of Labor’s FMLA Employer Guide provides a framework for implementing intermittent leave in small increments. When applied consistently, this approach keeps employees connected to the workforce and reduces the likelihood of extended disability leave.

Reasonable accommodations can help employees remain productive and safe. The Job Accommodation Network (JAN) Hemophilia Guide outlines practical options—such as flexible scheduling, reduced physical demands, and modified workspaces—that support employees while enabling them to perform essential job functions.

Employees caring for a child or family member with hemophilia often manage a significant “silent” workload, balancing treatment routines, medical appointments, and emotional stress. Resources such as Hope for Hemophilia and the Hemophilia Federation of America’s Mental Health Hub offer support programs that can reduce caregiver strain and help employees stay engaged at work.

Living with or caring for someone with hemophilia can contribute to anxiety, burnout, and financial stress. Employers that integrate mental health resources—EAP access, counseling, peer support, and condition specific education—can help employees navigate these challenges more effectively.

Hemophilia is rare, but its impact on cost, productivity, and employee well being is significant. Employers who understand the condition and implement proactive strategies—intermittent leave, ADA accommodations, caregiver support, and mental health resources—can reduce preventable disruptions, improve retention, and create a workplace environment that supports stability and long term success for employees and their families.

Because of the low prevalence of hemophilia, employers as a key payer group have very limited knowledge and receive minimal information from carriers, pharmacy benefit managers (PBMs), third-party administrators (TPAs), and pharmacy and medical consultants on best practices. Most often, employers receive information in a retrospective manner requiring them to respond after the condition presents in claims reports – leaving them without proactive strategies to manage care or spending.

The impact of complications, such as recurrent bleeding, affects the productivity of people with hemophilia and their caregivers, including:

  • 26 missed days per year at work/school
  • 20 low-productivity days per year
  • 19 missed days per year for caregivers
  • 19% of parents reported being underemployed due to their child's condition

Facts About Hemophilia

Clinically, people with hemophilia are lacking one or more important proteins called clotting factors. In the absence of these proteins, blood cannot clot normally. The specific type of hemophilia depends on which clotting factor is missing or deficient. People with hemophilia bleed longer than others after an injury or surgery and may also have internal bleeding that can damage organs and tissues and even be life-threatening. Women who inherit the hemophilia gene often have reduced clotting factor levels, which can lead to symptoms such as heavy periods, easy bruising, or bleeding into joints. In some cases, factor levels are low enough they meet the clinical criteria for a hemophilia diagnosis.

According to the National Bleeding Disorders Foundation (NCBD):

  • Family history of hemophilia is present in almost two-thirds of cases
  • Hemophilia occurs more commonly in males - 1 in every 5,617 male births
  • Primary symptoms are bleeding longer than other people; bleeds can occur internally, into joints and muscles, or externally, from minor cuts, dental procedures, or injuries
  • Bleeding can occur both externally and internally
  • Internal bleeding, which often happens in the space around the joints (especially the knee, elbow, ankle) and in muscles, frequently causes pain and swelling and can lead to decreased mobility and disability
  • Left untreated, bleeding can lead to permanent painful joint disease and sometimes death

Living with Hemophilia

“We want to make sure we’re focused on the whole patient and the family. In our case, it was two dependents who had hemophilia. For the family, how has this impacted the father’s ability to be effective at work? For the company, how has this impacted disability costs, lost workdays, productivity, etc.?”

- MBGH Employer Member


Living with hemophilia as an adult or as a primary caregiver can present psychosocial, physical and financial challenges. These challenges affect everything from activities of daily living to treatment adherence and work productivity. Managing hemophilia has a substantial impact on the patient and caregiver alike.

Members living with hemophilia can experience various access barriers that increase the burden of these challenges. Access barriers include:

  • Lack of timely access to medication due to prior authorization or utilization management design.
  • Copay accumulator adjusters create significant financial barriers to accessing medication, often leading to patients not filling their prescriptions and instead seeking treatment for bleeds at the emergency department.
  • Alternative funding programs leave patients in limbo for significant periods of time before either gaining access to medication through manufacturer patient assistance programs or worse - not qualifying for assistance and being left with no avenue to access lifesaving medications.
  • Delays in medication access due to specialty pharmacy processing/shipping time.

Currently there is no cure for hemophilia, but very effective treatments are available in the US, primarily involving acute care of bleeds when they occur (on demand) and regular administration of prophylaxis of factor replacement therapy or substitution therapy (a medication that acts as a substitute for clotting factor) to help prevent bleeds. Generally, the goal of treatment is to decrease the frequency and severity of bleeding episodes and prevent complications related to bleeding.

It is important for employers to be aware this condition can impact employees, their spouses and children, and/or caregivers. Hemophilia is a lifelong disease that requires intensive management, individualized care strategies and significant patient involvement – factors that make proactive employer strategies essential.

There are many layers to understanding a person living with hemophilia; employers with a hemophilia member on their plan can benefit greatly by contacting a local Hemophilia Treatment Center for expert advice on workplace safety, best in class care, and personalized training for their benefits and safety teams. Read more about living with hemophilia here.

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